Pompe Disease
Showing 1 - 25 of >10,000
Pompe Disease (Late-onset) Trial (No Intervention)
Not yet recruiting
- Pompe Disease (Late-onset)
- No Intervention
- (no location specified)
Nov 21, 2023
Pompe Disease Trial in New York, Fairfax (biological, drug, other)
Not yet recruiting
- Pompe Disease
- Cipaglucosidase alfa
- +3 more
-
New York, New York
- +1 more
Nov 2, 2023
Pompe Disease, Muscle Loss, Obesity Trial (Multi-ingredient supplement (PDT-MIS), Placebo (PLA))
Not yet recruiting
- Pompe Disease
- +7 more
- Multi-ingredient supplement (PDT-MIS)
- Placebo (PLA)
- (no location specified)
Nov 8, 2023
Pompe Disease -Non-invasive Magnetic Resonance Exploratory Pilot
Not yet recruiting
- Pompe Disease
- McArdle Disease
- Siemens Magnetom 7T Plus
-
Vienna, AustriaMedical University of Vienna
Jul 5, 2023
Patients With "Late-Onset" Pompe Disease
Active, not recruiting
- Pompe Disease
- +2 more
- Observational
-
Durham, North CarolinaDuke University
Oct 7, 2022
ERT in Pompe Disease: Elucidation of Molecular Structures
Not yet recruiting
- Pompe-Disease
-
Rüsselsheim, Hessen, GermanyCentre for Analytical Biochemistry
Jan 30, 2023
Pompe Disease Infantile-Onset Trial in China (GC301)
Not yet recruiting
- Pompe Disease Infantile-Onset
- GC301
-
Beijing, China
- +4 more
Apr 2, 2023
Late-onset Pompe Disease Trial in Gainesville, London (Respiratory muscle strength measurements by different techniques.)
Terminated
- Late-onset Pompe Disease
- Respiratory muscle strength measurements by different techniques.
-
Gainesville, Florida
- +1 more
Apr 11, 2022
Pompe Disease, Pompe Disease (Late-onset), Pompe's Disease Juvenile Onset Trial in Erlangen (Multispectral Optoacoustic
Recruiting
- Pompe Disease
- +3 more
- Multispectral Optoacoustic Tomography
-
Erlangen, Bavaria, GermanyUniversity Hospital Erlangen
Jun 2, 2022
Glycogen Storage Disease Type II, Pompe Disease (Late-onset) Trial in Milan (Inspiratory Muscle Training (IMT), Inspiratory
Recruiting
- Glycogen Storage Disease Type II
- Pompe Disease (Late-onset)
- Inspiratory Muscle Training (IMT)
- Inspiratory Muscle Training (IMT) + Air Stacking
-
Milan, ItalyIRCCS S. Maria Nascente - Fondazione Don Carlo Gnocchi
Jul 11, 2023
Pompe's Disease Trial in China (ALGLUCOSIDASE ALFA)
Recruiting
- Pompe's Disease
- ALGLUCOSIDASE ALFA
-
China, ChinaInvestigational Site
Oct 26, 2022
Cognitive and Neurological Pathologies in Pompe Disease
Recruiting
- Pompe Disease
-
Durham, North CarolinaDuke University Medical Center
Jun 30, 2022
Infantile-onset Pompe Disease Trial in Beijing (Genetic: GC301)
Recruiting
- Infantile-onset Pompe Disease
- Genetic: GC301
-
Beijing, Beijing, ChinaBayi Children's Hospital, Seventh Medical Center, PLA general ho
Sep 30, 2022
Pompe Disease (Late-onset) Trial in Durham (Clenbuterol, Placebos)
Withdrawn
- Pompe Disease (Late-onset)
- Clenbuterol
- Placebos
-
Durham, North CarolinaDuke University Medical Center
Aug 15, 2022
Pompe Disease, Glycogen Storage Disease Type II (GSD-II), Acid Maltase Deficiency Disease Trial in Gainesville, Decatur, Detroit
Completed
- Pompe Disease
- +2 more
- alglucosidase alfa
-
Gainesville, Florida
- +2 more
Jul 29, 2022
Late-Onset Pompe Disease, Lysosomal Disease Trial in Durham (IMT therapy using the Pr02 mobile device)
Recruiting
- Late-Onset Pompe Disease
- Lysosomal Disease
- IMT therapy using the Pr02 mobile device
-
Durham, North CarolinaDuke University Medical Center
Jul 21, 2022
Pompe Disease Trial in Saint Louis, New York, Durham (ACTUS-101)
Recruiting
- Pompe Disease
- ACTUS-101
-
Saint Louis, Missouri
- +2 more
May 25, 2022
Natural History of Pompe Disease
Recruiting
- Glycogen Storage Disease Type II, Adult
-
Garches, Hauts-de-Seine, FranceHôpital Raymond Poincaré
Apr 20, 2022
Pompe Disease Trial in Zürich (Testing of reliability / validity of new questionnaire)
Recruiting
- Pompe Disease
- Testing of reliability / validity of new questionnaire
-
Zürich, SwitzerlandUniversity Childrens Hospital Zürich
May 25, 2022
Pompe & Pain - Study to Assess Nociceptive Pain in Adult Pompe
Not yet recruiting
- Pompe Disease (Late-onset)
- +3 more
- Beck depression inventory fast screen (Questionnaire)
- +20 more
-
Munich, Bavaria, GermanyFriedrich-Baur-Institute, Dep. of Neurology Klinikum der Univers
Mar 8, 2022
Pompe Disease Trial in Gainesville (genetic, drug, other)
Completed
- Pompe Disease
- Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase
- +7 more
-
Gainesville, FloridaClinical and Translational Research Building (CTRB), University
Mar 24, 2022
Glycogen Storage Disease Type II Trial in Worldwide (Alglucosidase alfa GZ419829)
Recruiting
- Glycogen Storage Disease Type II
- Alglucosidase alfa GZ419829
-
Leuven, Belgium
- +8 more
Jan 17, 2023
Pompe Telemedicine Developmental Study
Completed
- Pompe Disease
- Glycogen Storage Disease II
-
Durham, North CarolinaDuke University Medical Center
Oct 27, 2021
Glycogen Storage Disease Type II Trial in France (Avalglucosidase alfa (GZ402666))
Recruiting
- Glycogen Storage Disease Type II
- Avalglucosidase alfa (GZ402666)
-
Brest, France
- +9 more
Jul 22, 2022